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Forbion Portfolio Company uniQure receives Approval for Glybera® First Gene Therapy by European Commission

noviembre 2, 2012

Human Health

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Forbion Capital Partners is pleased to announce that its investee company, uniQure received approval today from the European Commission (EC) for the gene therapy Glybera® (alipogene tiparvovec), a treatment for patients with lipoprotein lipase deficiency (LPLD, also called familial hyperchylomicronemia) suffering from recurring acute pancreatitis. Patients with LPLD, a very rare, inherited disease, are unable to metabolize the fat particles carried in their blood, which leads to inflammation of the pancreas (pancreatitis), an extremely serious, painful, and potentially lethal condition. The approval makes Glybera the first gene therapy approved by regulatory authorities in the Western world.